World Orphan Drug Congress Europe 2023
30 October - 2 November, 2023 | Booth # 70 | Fira de Barcelona Montjuic | Barcelona, Spain
Thank you for speaking with the ICON team at World Orphan Drug Congress 2023
We understand the unique strategic, operational, medical and scientific challenges that rare disease clinical trials present, and we invite you to explore how we are leading the way in Rare Disease drug development.
Contact usfor more information or to arrange a meeting with our experts.
Case studies:
Recruitment Challenges
Overcoming operational challenges and exceeding recruitment timeline in an adult patient population with Fibrodysplasia Ossificans Progressiva.
Decentralised Trials Rare Disease
Trial decentralisation enhances clinical research accessibility and reduces burden on rare disease patient population.
Whitepapers:
Natural history studies to improve drug development in rare diseases
Practical strategies for rare disease natural history studies, patient identification, recruitment and retention.
The key to remarkable rare disease registries
Building trust and collaboration with patient advocacy organisations.
Leveraging historical data for use in rare disease trials
Understanding the Bayesian and Frequentist approaches.
Rare Disease Crossing the finish line
Why effective participation support strategy is critical to trial efficiency and success in rare diseases.
Cross-border enrollment of rare disease patients
Considerations for planning and conducting global rare disease clinical trials.
Beyond buzzwords: Diversity, equity and inclusion in rare disease clinical trials
Focused effort and dedicated action are essential to create an equitable clinical research environment.
Mapi Research Trust: Facilitating access to Clinical Outcome Assessments (COA and eCOA) for the entire scientific community
Factsheet
Clinical Outcome Assessments (COAs) and patient-centric expertise for Rare Diseases
Brochure
ePROVIDETM: Helping you build your COA strategies.